What's Happening?
Medunik USA, a specialty pharmaceutical company, has reaffirmed its commitment to the sickle cell disease (SCD) community by ensuring an uninterrupted supply of Siklos®, a dissolvable formulation of hydroxyurea.
Siklos® is FDA-approved for reducing painful crises and blood transfusions in patients aged 2 years and older. Medunik USA has expanded its coverage under Medicaid Programs, with 13 states including Siklos® on their Preferred Drug List and 24 states reimbursing it with limited restrictions. The company also offers patient support services, including copay assistance and clinical guidance, to enhance accessibility and affordability.
Why It's Important?
Sickle cell anemia is the most common inherited blood disorder in the U.S., affecting nearly 100,000 Americans, primarily of African ancestry. It significantly reduces life expectancy and quality of life. Medunik USA's efforts to maintain the availability of Siklos® and expand access through Medicaid are crucial for ensuring that patients receive consistent and effective treatment. The company's patient-centered services further support individuals in managing the disease, highlighting the importance of equitable access to healthcare for rare diseases.
What's Next?
Medunik USA plans to continue supporting sickle cell advocacy organizations and expanding its patient-centered services. The company is committed to improving the health and quality of life for patients with rare diseases by making orphan drug therapies more accessible. Future efforts may include further expansion of Medicaid coverage and enhancement of patient support programs.
Beyond the Headlines
The focus on rare diseases and orphan drugs underscores the challenges faced by patients with conditions that have limited treatment options. Medunik USA's approach highlights the need for pharmaceutical companies to prioritize accessibility and affordability, particularly for underserved communities. This commitment to patient-centered care can serve as a model for other companies in the industry.











